Gene Therapy in Patients with Limb-Girdle Muscular Dystrophy Type 2E




Neurology Minute show

Summary: Dr. Louise Rodino-Klapac discusses her abstract, "Safety, β-sarcoglycan Expression and Functional Outcomes from Systemic Gene Transfer of rAAVrh74.MHCK7.SGCB in Patients with Limb-Girdle Muscular Dystrophy Type 2E (LGMD2E)". You can view her abstract and others here: https://index.mirasmart.com/AAN2021/